# A PHASE 1/2 OPEN LABEL EXTENSION STUDY OF GIVOSIRAN, AN INVESTIGATIONAL RNAI THERAPEUTIC, IN PATIENTS WITH ACUTE INTERMITTENT PORPHYRIA

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/a-phase-1-2-open-label-extension-study-of-givosiran-an-investigational-rnai/

## Facts

| Field | Value |
| --- | --- |
| Author Names | R. De Marchi,Leila Duarte,Sudhir Kumar Paidesetty,Rithesh Patel M D,Andersen Ke,Bonkovsky HL,S. E,Hemadharsni.P Hemadharsni.P,B. M,E. Al |
| Citations | 5 |
| DOI | 10.1016/j.htct.2020.10.028 |
| Fields | Biochemistry, Genetics and Molecular Biology,Medicine |
| Open Access | true |
| OA Status | diamond |
| OA URL | https://doi.org/10.1016/j.htct.2020.10.028 |
| OpenAlex ID | https://openalex.org/W3097915935 |
| Type | article |
| Year | 2020 |

## Paper authors

- [Leila Duarte](https://scholariq.org/researchers/leila-duarte/)

## Paper primary topic

- [Porphyrin Metabolism and Disorders](https://scholariq.org/topics/porphyrin-metabolism-and-disorders/)

## Paper topics

- [Porphyrin Metabolism and Disorders](https://scholariq.org/topics/porphyrin-metabolism-and-disorders/)
- [Metabolism and Genetic Disorders](https://scholariq.org/topics/metabolism-and-genetic-disorders/)
- [Folate and B Vitamins Research](https://scholariq.org/topics/folate-and-b-vitamins-research/)

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