# A Phase 3 Trial of Sebelipase Alfa in Lysosomal Acid Lipase Deficiency

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/a-phase-3-trial-of-sebelipase-alfa-in-lysosomal-acid-lipase-deficiency/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Barbara K. Burton,Manisha Balwani,François Feillet,Ivo Barić,T. Burrow,C. Camarena Grande,Mahmut Çöker,Alejandra Consuelo‐Sánchez,Patrick Deegan,Maja Di Rocco,Gregory M. Enns,Richard W. Erbe,Fatih Süheyl Ezgü,Can Fıçıcıoğlu,Katryn N. Furuya,John P. Kane,Christina M. Laukaitis,Eugen Mengel,Edward Neilan,S. L. Nightingale,Heidi Peters,Maurizio Scarpa,Karl Otfried Schwab,Vratislav Smolka,Vassili Valayannopoulos,Marnie J. Wood,Zachary Goodman,Yijun Yang,Stephen Eckert,Sandra Rojas-Caro,Anthony Quinn |
| Citations | 247 |
| DOI | 10.1056/nejmoa1501365 |
| Fields | Medicine |
| Open Access | true |
| OA Status | bronze |
| OA URL | https://www.nejm.org/doi/pdf/10.1056/NEJMoa1501365?articleTools=true |
| OpenAlex ID | https://openalex.org/W2328315454 |
| PMID | 26352813 |
| Type | article |
| Year | 2015 |

## Paper authors

- [Vassili Valayannopoulos](https://scholariq.org/researchers/vassili-valayannopoulos/)

## Paper journal

- [New England Journal of Medicine](https://scholariq.org/journals/new-england-journal-of-medicine/)

## Paper primary topic

- [Lysosomal Storage Disorders Research](https://scholariq.org/topics/lysosomal-storage-disorders-research/)

## Paper topics

- [Lysosomal Storage Disorders Research](https://scholariq.org/topics/lysosomal-storage-disorders-research/)
- [Biomedical Research and Pathophysiology](https://scholariq.org/topics/biomedical-research-and-pathophysiology/)
- [Glycogen Storage Diseases and Myoclonus](https://scholariq.org/topics/glycogen-storage-diseases-and-myoclonus/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.