# A randomized placebo-controlled phase 3 trial of an antisense oligonucleotide, drisapersen, in Duchenne muscular dystrophy

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/a-randomized-placebo-controlled-phase-3-trial-of-an-antisense-oligonucleotide/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Nathalie Goemans,Eugenio Mercuri,Е. Д. Белоусова,Hirofumi Komaki,Alberto Dubrovsky,Craig M. McDonald,John E. Kraus,Afrodite Lourbakos,Zhengning Lin,Giles Campion,Susanne X. Wang,Craig Campbell,Abelardo Araújo,Enrico Bertini,Peter Born,Claude Cancés,B. Chabrol,Jong‐Hee Chae,J. Colomer Oferil,Giacomo P. Comi,J. Cuisset,Guy D’Anjou,Isabelle Desguerre,Ricardo Erazo Torricelli,Raúl G. Escobar,David Feder,Alessandra Ferlini,Roberto Giugliani,Erik Henricson,Ágnes Herczegfalvi,Yuh‐Jyh Jong,Shigemi Kimura,Janbernd Kirschner,Karin Kleinsteuber,Anna Kostera‐Pruszczyk,Martin Kudr,Wolfgang Mueller‐Felber,E. Niks,Katsuhisa Ogata,Concetta Palermo,Marika Pane,Samuel Ignacio Pascual Pascual,Yann Péréon,Salmo Raskin,Magnhild Rasmussen,U.C. Reed,Ulrike Schara,Kathryn Selby,Cláudia Ferreira da Rosa Sobreira,Yasuhiro Takeshima,J.J. Vilchez Padilla,Gian Luca Vita,Petr Vondráček,Gert Wiegand,Ekkehard Wilichowski |
| Citations | 128 |
| DOI | 10.1016/j.nmd.2017.10.004 |
| Fields | Biochemistry, Genetics and Molecular Biology,Medicine |
| Open Access | true |
| OA Status | hybrid |
| OA URL | http://www.nmd-journal.com/article/S0960896617302006/pdf |
| OpenAlex ID | https://openalex.org/W2774788400 |
| PMID | 29203355 |
| Type | article |
| Year | 2017 |

## Paper authors

- [Jong‐Hee Chae](https://scholariq.org/researchers/jong-hee-chae/)

## Paper primary topic

- [Muscle Physiology and Disorders](https://scholariq.org/topics/muscle-physiology-and-disorders/)

## Paper topics

- [Muscle Physiology and Disorders](https://scholariq.org/topics/muscle-physiology-and-disorders/)
- [Neurogenetic and Muscular Disorders Research](https://scholariq.org/topics/neurogenetic-and-muscular-disorders-research/)
- [Telomeres, Telomerase, and Senescence](https://scholariq.org/topics/telomeres-telomerase-and-senescence/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.
