# Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/ataluren-in-patients-with-nonsense-mutation-duchenne-muscular-dystrophy-act-dmd/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Craig M. McDonald,Craig Campbell,Ricardo Erazo Torricelli,Richard S. Finkel,Kevin M. Flanigan,Nathalie Goemans,Peter Heydemann,Anna Kamińska,Janbernd Kirschner,Francesco Muntoni,A. Nascimento Osorio,Ulrike Schara,Thomas Sejersen,Perry B. Shieh,H. Lee Sweeney,Haluk Topaloğlu,M. Tulinius,Juan J. Vílchez,Thomas Voït,Brenda Wong,Gary Elfring,Hans Kröger,Xiaohui Luo,Joseph McIntosh,Tuyen Ong,Peter Riebling,Marcio Ferreira de Souza,Robert J. Spiegel,Stuart W. Peltz,Eugenio Mercuri,Lindsay N. Alfano,Michelle Eagle,M. James,Linda Lowes,Anna Mayhew,Elena Mazzone,Leslie Nelson,Kristy Rose,Hoda Abdel‐Hamid,Susan Apkon,Richard J. Barohn,Enrico Bertini,Clemens Bloetzer,Lausanne Canton de Vaud,Russell J. Butterfield,B. Chabrol,Jong‐Hee Chae,Daehak-ro Jongno-gu,Giacomi Pietro Comi,Basil T. Darras,Jahannaz Dastgir,Isabelle Desguerre,Raúl G. Escobar,Erika Finanger,Michela Guglieri,Imelda Hughes,Susan T. Iannaccone,Kristi Jones,Peter Karachunski,Martin Kudr,Timothy Lotze,Jean K. Mah,Katherine D. Mathews,Yoram Nevo,Julie Parsons,Yann Péréon,Alexandra Prufer de Queiroz Campos Araújo,J. Ben Renfroe,Maria Bernadete Dutra de Resende,Monique M. Ryan,Kathryn Selby,Gihan Tennekoon,Giuseppe Vita |
| Citations | 459 |
| DOI | 10.1016/s0140-6736(17)31611-2 |
| Fields | Biochemistry, Genetics and Molecular Biology,Medicine |
| Open Access | true |
| OA Status | bronze |
| OA URL | http://www.thelancet.com/article/S0140673617316112/pdf |
| OpenAlex ID | https://openalex.org/W2735778907 |
| PMID | 28728956 |
| Type | article |
| Year | 2017 |

## Paper authors

- [Janbernd Kirschner](https://scholariq.org/researchers/janbernd-kirschner/)
- [Jong‐Hee Chae](https://scholariq.org/researchers/jong-hee-chae/)
- [Thomas Sejersen](https://scholariq.org/researchers/thomas-sejersen/)

## Paper journal

- [The Lancet](https://scholariq.org/journals/the-lancet/)

## Paper primary topic

- [Muscle Physiology and Disorders](https://scholariq.org/topics/muscle-physiology-and-disorders/)

## Paper topics

- [Muscle Physiology and Disorders](https://scholariq.org/topics/muscle-physiology-and-disorders/)
- [Adipose Tissue and Metabolism](https://scholariq.org/topics/adipose-tissue-and-metabolism/)
- [Neurogenetic and Muscular Disorders Research](https://scholariq.org/topics/neurogenetic-and-muscular-disorders-research/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.