# Clinical outcomes after long-term treatment with alglucosidase alfa in infants and children with advanced Pompe disease

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/clinical-outcomes-after-long-term-treatment-with-alglucosidase-alfa-in-infants/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Marc Nicolino,Barry J. Byrne,J. Edmund Wraith,Nancy Leslie,Hanna Mandel,David R. Freyer,Georgianne L. Arnold,Enikö K. Pivnick,C. J. Ottinger,Peter H. Robinson,John-Charles A. Loo,Martin Smitka,Philip Jardine,Luciano Tatò,B. Chabrol,Shawn E. McCandless,Shigemi Kimura,Lakshmi Mehta,Deeksha Bali,Alison Skrinar,Claire Morgan,Lakshmi Rangachari,Deya Corzo,Priya S. Kishnani |
| Citations | 292 |
| DOI | 10.1097/gim.0b013e31819d0996 |
| Fields | Chemistry,Medicine |
| Open Access | true |
| OA Status | bronze |
| OA URL | http://www.gimjournal.org/article/S1098360021026435/pdf |
| OpenAlex ID | https://openalex.org/W2055655054 |
| PMID | 19287243 |
| Type | article |
| Year | 2009 |

## Paper authors

- [David R. Freyer](https://scholariq.org/researchers/david-r-freyer/)

## Paper primary topic

- [Lysosomal Storage Disorders Research](https://scholariq.org/topics/lysosomal-storage-disorders-research/)

## Paper topics

- [Lysosomal Storage Disorders Research](https://scholariq.org/topics/lysosomal-storage-disorders-research/)
- [Glycogen Storage Diseases and Myoclonus](https://scholariq.org/topics/glycogen-storage-diseases-and-myoclonus/)
- [Carbohydrate Chemistry and Synthesis](https://scholariq.org/topics/carbohydrate-chemistry-and-synthesis/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.