# Clinical Outcomes in Duchenne Muscular Dystrophy: A Study of 5345 Patients from the TREAT-NMD DMD Global Database

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/clinical-outcomes-in-duchenne-muscular-dystrophy-a-study-of-5345-patients-from/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Zaïda Koeks,Catherine L. Bladen,David Salgado,Erik W. van Zwet,Oksana Pogoryelova,Grace McMacken,Soledad Monges,María Eugenia Foncuberta,Kyriaki Kekou,Konstantina Kosma,Hugh Dawkins,Leanne Lamont,M. Bellgard,Anna J. Roy,Teodora Chamova,Velina Guergueltcheva,H.S. Chan,Lawrence Korngut,Craig Campbell,Yi Dai,Jen Wang,Nina Barišić,Petr Brabec,Jaana Lähdetie,Maggie C. Walter,Olivia Schreiber‐Katz,Veronika Karcagi,Marta Garami,Ágnes Herczegfalvi,Venkatarman Viswanathan,Farhad Bayat,Filippo Buccella,Alessandra Ferlini,En Kimura,J.C. van den Bergen,Miriam Rodrigues,Richard Roxburgh,Anna Łusakowska,Anna Kostera‐Pruszczyk,Rosário Santos,Elena Neagu,Svetlana Artemieva,Vedrana Milić Rašić,Dina Vojinović,Manuel Posada de la Paz,Clemens Bloetzer,Andrea Klein,Jordi Díaz‐Manera,Eduard Gallardo,Aynur Ayşe Karaduman,Tunca Oznur,Haluk Topaloğlu,Rasha El Sherif,Angela Stringer,Andriy Shatillo,Ann Martin,Holly L. Peay,Janbernd Kirschner,Kevin M. Flanigan,Volker Straub,Kate Bushby,Christophe Béroud,Jan J.G.M. Verschuuren,Hanns Lochmüller |
| Citations | 184 |
| DOI | 10.3233/jnd-170280 |
| Fields | Biochemistry, Genetics and Molecular Biology,Medicine |
| Open Access | true |
| OA Status | bronze |
| OA URL | https://content.iospress.com:443/download/journal-of-neuromuscular-diseases/jnd170280?id=journal-of-neuromuscular-diseases%2Fjnd170280 |
| OpenAlex ID | https://openalex.org/W2767327591 |
| PMID | 29125504 |
| Type | article |
| Year | 2017 |

## Paper authors

- [Janbernd Kirschner](https://scholariq.org/researchers/janbernd-kirschner/)
- [Olivia Schreiber‐Katz](https://scholariq.org/researchers/olivia-schreiber-katz/)
- [Hanns Lochmüller](https://scholariq.org/researchers/hanns-lochmuller/)

## Paper journal

- [Journal of Neuromuscular Diseases](https://scholariq.org/journals/journal-of-neuromuscular-diseases/)

## Paper primary topic

- [Muscle Physiology and Disorders](https://scholariq.org/topics/muscle-physiology-and-disorders/)

## Paper topics

- [Muscle Physiology and Disorders](https://scholariq.org/topics/muscle-physiology-and-disorders/)
- [Cardiomyopathy and Myosin Studies](https://scholariq.org/topics/cardiomyopathy-and-myosin-studies/)
- [Neurogenetic and Muscular Disorders Research](https://scholariq.org/topics/neurogenetic-and-muscular-disorders-research/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.
