# Early experience with compassionate use of 2 hydroxypropyl-beta-cyclodextrin for Niemann–Pick type C disease: review of initial published cases

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/early-experience-with-compassionate-use-of-2-hydroxypropyl-beta-cyclodextrin-for/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Juan Eduardo Megías‐Vericat,Ana García‐Robles,María José Fernández-Megía,Francisco Pérez‐Miralles,Eduardo López Briz,Bonaventura Casanova,José Luís Poveda |
| Citations | 36 |
| DOI | 10.1007/s10072-017-2833-9 |
| Fields | Medicine |
| Open Access | true |
| OA Status | green |
| OA URL | https://hdl.handle.net/10550/122589 |
| OpenAlex ID | https://openalex.org/W2584314070 |
| PMID | 28155026 |
| Type | article |
| Year | 2017 |

## Paper authors

- [Eduardo López Briz](https://scholariq.org/researchers/eduardo-lopez-briz/)

## Paper primary topic

- [Lysosomal Storage Disorders Research](https://scholariq.org/topics/lysosomal-storage-disorders-research/)

## Paper topics

- [Lysosomal Storage Disorders Research](https://scholariq.org/topics/lysosomal-storage-disorders-research/)
- [Child Nutrition and Feeding Issues](https://scholariq.org/topics/child-nutrition-and-feeding-issues/)
- [Autoimmune and Inflammatory Disorders Research](https://scholariq.org/topics/autoimmune-and-inflammatory-disorders-research/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.