# Effect of an intravitreal antisense oligonucleotide on vision in Leber congenital amaurosis due to a photoreceptor cilium defect

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/effect-of-an-intravitreal-antisense-oligonucleotide-on-vision-in-leber/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Artur V. Cideciyan,Samuel G. Jacobson,Arlene V. Drack,Allen C. Ho,Jason Charng,Alexandra V. Garafalo,Alejandro J. Román,Alexander Sumaroka,Ian C. Han,Maria D. Hochstedler,Wanda Pfeifer,Elliott H. Sohn,Magali Taiel,Michael R. Schwartz,Patricia Biasutto,Wilma de Wit,Michael E. Cheetham,Peter Adamson,David M. Rodman,Gerard Platenburg,Maria D. Tome,Irina Balikova,Fanny Nerinckx,Julie De Zaeytijd,Caroline Van Cauwenbergh,Bart P. Leroy,Stephen R. Russell |
| Citations | 219 |
| DOI | 10.1038/s41591-018-0295-0 |
| Fields | Biochemistry, Genetics and Molecular Biology,Medicine |
| Open Access | true |
| OA Status | bronze |
| OA URL | https://www.nature.com/articles/s41591-018-0295-0.pdf |
| OpenAlex ID | https://openalex.org/W2903772223 |
| PMID | 30559420 |
| Type | article |
| Year | 2018 |

## Paper authors

- [Wanda Pfeifer](https://scholariq.org/researchers/wanda-pfeifer/)

## Paper journal

- [Nature Medicine](https://scholariq.org/journals/nature-medicine/)

## Paper primary topic

- [Retinal Development and Disorders](https://scholariq.org/topics/retinal-development-and-disorders/)

## Paper topics

- [Retinal Development and Disorders](https://scholariq.org/topics/retinal-development-and-disorders/)
- [Corneal Surgery and Treatments](https://scholariq.org/topics/corneal-surgery-and-treatments/)
- [Corneal surgery and disorders](https://scholariq.org/topics/corneal-surgery-and-disorders/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.