# Effect of nusinersen on motor, respiratory and bulbar function in early-onset spinal muscular atrophy

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/effect-of-nusinersen-on-motor-respiratory-and-bulbar-function-in-early-onset/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Astrid Pechmann,Max Behrens,Katharina Dörnbrack,Adrian Tassoni,Sabine Stein,Sibylle Emilie Vogt,Daniela Zöller,Günther Bernert,Tim Hagenacker,Ulrike Schara‐Schmidt,Inge Schwersenz,Maggie C. Walter,Matthias Baumann,Manuela Baumgärtner,Marcus Deschauer,Astrid Eisenkölbl,Marina Flotats‐Bastardas,Andreas Hahn,Veronka Horber,Ralf A. Husain,Sabine Illsinger,Jessika Johannsen,Cornelia Köhler,Heike Kölbel,Monika Müller,Arpad von Moers,Kurt Schlachter,Gudrun Schreiber,Oliver Schwartz,Martin Smitka,Elisabeth Steiner,Eva Stögmann,Regina Trollmann,Katharina Vill,Claudia Weiß,Gert Wiegand,Andreas Ziegler,Hanns Lochmüller,Janbernd Kirschner,the SMArtCARE study group,Thea Beatrice Abele,Bárbara Andres,Daniela Angelova-Toshkina,Petra Baum,Tobias Baum,Ute Baur,Benedikt Becker,Bettina Behring,Theresa Birsak,Julia Bellut,Astrid Bertsche,Markus Blankenburg,Astrid Blaschek,Nathalie Braun,Sarah Braun,Nadine Burgenmeister,Nicole Claus,Isabell Cordts,Heike de Vries,Timo Deba,Adela Della Marina,Jonas Denecke,Joenna Driemeyer,Matthias Eckenweiler,Barbara Fiedler,Michal Fischer,Maren Freigang,Johannes Friese,Philippa Gaiser,Axel Gebert,Stephanie Geitmann,Klaus Goldhahn,Michael Grässl,Kristina Gröning,Julian Großkreutz,U Gruber‐Sedlmayr,Helene Guillemot,René Günther,Maja von der Hagen,H. Hartmann,Miriam Hiebeler,Elke Hobbiebrunken,Georg F. Hoffmann,Britta Holtkamp,Dorothea Holzwarth,Eva Jansen,Angela M. Kaindl,Nadja Kaiser,Jennifer Klamroth,Jan Christoph Koch,Stefan Koelker,Kirsten Kolzter,Brigitte Korschinsky,Hanna Küpper,Thorsten Langer,Ilka Lehnert,Paul Lingor,Wolfgang N. Löscher,Dana Loudovici-Krug,Κyriakos Martakis |
| Citations | 72 |
| DOI | 10.1093/brain/awac252 |
| Fields | Biochemistry, Genetics and Molecular Biology,Medicine |
| Open Access | true |
| OA Status | bronze |
| OA URL | https://academic.oup.com/brain/article-pdf/146/2/668/49171648/awac252.pdf |
| OpenAlex ID | https://openalex.org/W4286008638 |
| PMID | 35857854 |
| Type | article |
| Year | 2022 |

## Paper authors

- [Moritz Metelmann](https://scholariq.org/researchers/moritz-metelmann/)

## Paper journal

- [Brain](https://scholariq.org/journals/brain/)

## Paper primary topic

- [Neurogenetic and Muscular Disorders Research](https://scholariq.org/topics/neurogenetic-and-muscular-disorders-research/)

## Paper topics

- [Neurogenetic and Muscular Disorders Research](https://scholariq.org/topics/neurogenetic-and-muscular-disorders-research/)
- [RNA modifications and cancer](https://scholariq.org/topics/rna-modifications-and-cancer/)
- [Congenital Anomalies and Fetal Surgery](https://scholariq.org/topics/congenital-anomalies-and-fetal-surgery/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.
