# Efficacy and safety of enzyme replacement therapy with BMN 110 (elosulfase alfa) for Morquio A syndrome (mucopolysaccharidosis IVA): a phase 3 randomised placebo‐controlled study

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/efficacy-and-safety-of-enzyme-replacement-therapy-with-bmn-110-elosulfase-alfa/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Christian J. Hendriksz,Barbara K. Burton,Thomas R. Fleming,Paul Harmatz,Derralynn Hughes,Simon Jones,Hsiang‐Yu Lin,Eugen Mengel,Maurizio Scarpa,Vassili Valayannopoulos,Roberto Giugliani,STRIVE Investigators,Peter Slasor,Debra L. Lounsbury,Wolfgang Dummer |
| Citations | 211 |
| DOI | 10.1007/s10545-014-9715-6 |
| Fields | Agricultural and Biological Sciences,Medicine |
| Open Access | true |
| OA Status | hybrid |
| OA URL | https://doi.org/10.1007/s10545-014-9715-6 |
| OpenAlex ID | https://openalex.org/W2127364492 |
| PMID | 24810369 |
| Type | article |
| Year | 2014 |

## Paper authors

- [Vassili Valayannopoulos](https://scholariq.org/researchers/vassili-valayannopoulos/)

## Paper primary topic

- [Lysosomal Storage Disorders Research](https://scholariq.org/topics/lysosomal-storage-disorders-research/)

## Paper topics

- [Lysosomal Storage Disorders Research](https://scholariq.org/topics/lysosomal-storage-disorders-research/)
- [Phytochemistry Medicinal Plant Applications](https://scholariq.org/topics/phytochemistry-medicinal-plant-applications/)
- [Parasitic Diseases Research and Treatment](https://scholariq.org/topics/parasitic-diseases-research-and-treatment/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.