# Efficacy and safety of once-daily nitisinone for patients with alkaptonuria (SONIA 2): an international, multicentre, open-label, randomised controlled trial

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/efficacy-and-safety-of-once-daily-nitisinone-for-patients-with-alkaptonuria/

## Facts

| Field | Value |
| --- | --- |
| Author Names | L. Ranganath,Eftychia Eirini Psarelli,Jean-Baptiste Arnoux,Daniela Braconi,Michael Briggs,Anders Bröijersén,Nadia Loftus,Helen Bygott,Trevor F. Cox,Andrew Davison,J.P. Dillon,Michael Fisher,Richard J. Fitzgerald,Federica Genovese,Helena Glasová,Anthony K Hall,Andrew T. Hughes,Juliette H. Hughes,Richard Imrich,Jonathan C. Jarvis,Milad Khedr,Dinny Laan,Kim‐Hanh Le Quan Sang,Emily Luangrath,Oľga Lukáčová,Anna M. Milan,Alpesh Mistry,Vanda Mlynáriková,Brendan P. Norman,Birgitta Olsson,Nicholas P Rhodes,Jozef Rovenský,Mattias Rudebeck,Annalisa Santucci,Ella Shweihdi,Ciarán Scott,Jana Sedláková,Nicolas Sireau,Roman Stančík,Johan Szamosi,Sophie Taylor,Christa van Kan,Sobhan Vinjamuri,Eva Vrtíková,Chris Webb,Elizabeth A. West,E. Záňová,Andrea Zaťková,James A. Gallagher |
| Citations | 126 |
| DOI | 10.1016/s2213-8587(20)30228-x |
| Fields | Biochemistry, Genetics and Molecular Biology,Medicine |
| Open Access | true |
| OA Status | green |
| OA URL | https://hdl.handle.net/11365/1115671 |
| OpenAlex ID | https://openalex.org/W3076782376 |
| PMID | 32822600 |
| Type | article |
| Year | 2020 |

## Paper authors

- [Federica Genovese](https://scholariq.org/researchers/federica-genovese/)

## Paper journal

- [The Lancet Diabetes & Endocrinology](https://scholariq.org/journals/the-lancet-diabetes-and-endocrinology/)

## Paper primary topic

- [Metabolism and Genetic Disorders](https://scholariq.org/topics/metabolism-and-genetic-disorders/)

## Paper topics

- [Metabolism and Genetic Disorders](https://scholariq.org/topics/metabolism-and-genetic-disorders/)
- [Adrenal Hormones and Disorders](https://scholariq.org/topics/adrenal-hormones-and-disorders/)
- [Blood disorders and treatments](https://scholariq.org/topics/blood-disorders-and-treatments/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.