# Efficacy and Safety of Vamorolone vs Placebo and Prednisone Among Boys With Duchenne Muscular Dystrophy

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/efficacy-and-safety-of-vamorolone-vs-placebo-and-prednisone-among-boys-with/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Michela Guglieri,Paula R. Clemens,Seth J. Perlman,Edward C. Smith,Iain Horrocks,Richard S. Finkel,Jean K. Mah,Nicolas Deconinck,Nathalie Goemans,Jana Haberlová,Volker Straub,L. Mengle-Gaw,Benjamin D. Schwartz,Amy D. Harper,Perry B. Shieh,Liesbeth De Waele,Diana Castro,Michelle Yang,Monique M. Ryan,Craig M. McDonald,M. Tulinius,Richard Webster,Hugh J. McMillan,Nancy L. Kuntz,Vashmi K. Rao,Giovanni Baranello,Stefan Spinty,Anne‐Marie Childs,Annie M. Sbrocchi,Kathryn Selby,Migvis Monduy,Yoram Nevo,Juan J. Vílchez,Andres Nascimento-Osorio,E. Niks,Imelda J. M. de Groot,Marina Katsalouli,M. James,Johannes van den Anker,Jesse M. Damsker,Alexandra Ahmet,Leanne M. Ward,Mark Jaros,Phil Shale,Utkarsh J. Dang,Eric P. Hoffman |
| Citations | 132 |
| DOI | 10.1001/jamaneurol.2022.2480 |
| Fields | Biochemistry, Genetics and Molecular Biology,Medicine,Neuroscience |
| Open Access | true |
| OA Status | hybrid |
| OA URL | https://jamanetwork.com/journals/jamaneurology/articlepdf/2795868/jamaneurology_guglieri_2022_oi_220049_1664471626.01632.pdf |
| OpenAlex ID | https://openalex.org/W4293458353 |
| PMID | 36036925 |
| Type | article |
| Year | 2022 |

## Paper authors

- [Hugh J. McMillan](https://scholariq.org/researchers/hugh-j-mcmillan/)

## Paper journal

- [JAMA Neurology](https://scholariq.org/journals/jama-neurology/)

## Paper primary topic

- [Muscle Physiology and Disorders](https://scholariq.org/topics/muscle-physiology-and-disorders/)

## Paper topics

- [Muscle Physiology and Disorders](https://scholariq.org/topics/muscle-physiology-and-disorders/)
- [Neurogenetic and Muscular Disorders Research](https://scholariq.org/topics/neurogenetic-and-muscular-disorders-research/)
- [Genetic Neurodegenerative Diseases](https://scholariq.org/topics/genetic-neurodegenerative-diseases/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.