# Enzyme replacement therapy in late‐onset Pompe's disease: A three‐year follow‐up

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/enzyme-replacement-therapy-in-late-onset-pompe-s-disease-a-three-year-follow-up/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Léon P. F. Winkel,Johanna M. P. van den Hout,Joep H. J. Kamphoven,Janus A. M. Disseldorp,Maaike Remmerswaal,Willem F. Arts,Maarten J. J. E. Loonen,Arnold G. Vulto,Pieter A. van Doorn,Gerard De Jong,Wim Hop,Gerrit Smit,Stuart K. Shapira,Marijke A. Boer,Arnold Reuser,Ans T. van der Ploeg,Otto P. van Diggelen |
| Citations | 231 |
| DOI | 10.1002/ana.20019 |
| Fields | Medicine |
| Open Access | false |
| OA Status | closed |
| OpenAlex ID | https://openalex.org/W2001805850 |
| PMID | 15048888 |
| Type | article |
| Year | 2004 |

## Paper authors

- [Arnold G. Vulto](https://scholariq.org/researchers/arnold-g-vulto/)

## Paper journal

- [Annals of Neurology](https://scholariq.org/journals/annals-of-neurology/)

## Paper primary topic

- [Lysosomal Storage Disorders Research](https://scholariq.org/topics/lysosomal-storage-disorders-research/)

## Paper topics

- [Lysosomal Storage Disorders Research](https://scholariq.org/topics/lysosomal-storage-disorders-research/)
- [Glycogen Storage Diseases and Myoclonus](https://scholariq.org/topics/glycogen-storage-diseases-and-myoclonus/)
- [Child Nutrition and Feeding Issues](https://scholariq.org/topics/child-nutrition-and-feeding-issues/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.
