# European Medicines Agency review of ataluren for the treatment of ambulant patients aged 5 years and older with Duchenne muscular dystrophy resulting from a nonsense mutation in the dystrophin gene

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/european-medicines-agency-review-of-ataluren-for-the-treatment-of-ambulant/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Manuel Haas,Viktor Vlcek,Pavel Balabanov,Tomas Salmonson,Serge Bakchine,Greg Markey,Martina Weise,Gabriele Schlosser‐Weber,Henning Brohmann,Concepción Prieto Yerro,Macarena Rodríguez-Mendizábal,Violeta Stoyanova‐Beninska,Hans L. Hillege |
| Citations | 160 |
| DOI | 10.1016/j.nmd.2014.11.011 |
| Fields | Biochemistry, Genetics and Molecular Biology,Medicine |
| Open Access | false |
| OA Status | closed |
| OpenAlex ID | https://openalex.org/W2005330089 |
| PMID | 25497400 |
| Type | article |
| Year | 2014 |

## Paper authors

- [Serge Bakchine](https://scholariq.org/researchers/serge-bakchine/)

## Paper primary topic

- [Muscle Physiology and Disorders](https://scholariq.org/topics/muscle-physiology-and-disorders/)

## Paper topics

- [Muscle Physiology and Disorders](https://scholariq.org/topics/muscle-physiology-and-disorders/)
- [Cardiomyopathy and Myosin Studies](https://scholariq.org/topics/cardiomyopathy-and-myosin-studies/)
- [Neurogenetic and Muscular Disorders Research](https://scholariq.org/topics/neurogenetic-and-muscular-disorders-research/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.