# Gene Therapy for Mitochondrial Disease by Delivering Restriction Endonuclease &lt;i&gt;Sma&lt;/i&gt;I into Mitochondria

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/gene-therapy-for-mitochondrial-disease-by-delivering-restriction-endonuclease/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Masashi Tanaka,Harm-Jan Borgeld,Jin Zhang,Shin‐ichi Muramatsu,Jian‐Sheng Gong,Makoto Yoneda,Wakako Maruyama,Makoto Naoi,Tohru Ibi,Ko Sahashi,Masayo Shamoto,Noriyuki Fuku,Miyuki Kurata,Yoshiji Yamada,Kumi Nishizawa,Yukihiro Akao,Nobuko Ohishi,Shigeaki Miyabayashi,Hiraku Umemoto,Tatsuo Muramatsu,Koichi Furukawa,Akihiko Kikuchi,Imaharu Nakano,Keiya Ozawa,Kunio Yagi |
| Citations | 211 |
| DOI | 10.1159/000064726 |
| Fields | Biochemistry, Genetics and Molecular Biology |
| Open Access | false |
| OA Status | closed |
| OpenAlex ID | https://openalex.org/W2050871996 |
| PMID | 12372991 |
| Type | article |
| Year | 2002 |

## Paper authors

- [Keiya Ozawa](https://scholariq.org/researchers/keiya-ozawa/)

## Paper journal

- [Journal of Biomedical Science](https://scholariq.org/journals/journal-of-biomedical-science/)

## Paper primary topic

- [Mitochondrial Function and Pathology](https://scholariq.org/topics/mitochondrial-function-and-pathology/)

## Paper topics

- [Mitochondrial Function and Pathology](https://scholariq.org/topics/mitochondrial-function-and-pathology/)
- [ATP Synthase and ATPases Research](https://scholariq.org/topics/atp-synthase-and-atpases-research/)
- [Metabolism and Genetic Disorders](https://scholariq.org/topics/metabolism-and-genetic-disorders/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.
