# Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/hematopoietic-stem-cell-gene-therapy-for-cerebral-adrenoleukodystrophy/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Florian Eichler,Christine Duncan,Patricia L. Musolino,Paul J. Orchard,Satiro De Oliveira,Adrian J. Thrasher,Myriam Armant,Colleen Dansereau,Troy C. Lund,Weston P. Miller,Gerald V. Raymond,Raman Sankar,Ami J. Shah,Caroline Sevin,H. Bobby Gaspar,Paul Gissen,Hernán Amartino,Drago Bratkovic,Nicholas Smith,Asif Paker,Esther Shamir,Tara O’Meara,David Davidson,Patrick Aubourg,David A. Williams |
| Citations | 599 |
| DOI | 10.1056/nejmoa1700554 |
| Fields | Biochemistry, Genetics and Molecular Biology,Medicine |
| Open Access | false |
| OA Status | closed |
| OpenAlex ID | https://openalex.org/W2764213443 |
| PMID | 28976817 |
| Type | article |
| Year | 2017 |

## Paper authors

- [Paul J. Orchard](https://scholariq.org/researchers/paul-j-orchard/)

## Paper journal

- [New England Journal of Medicine](https://scholariq.org/journals/new-england-journal-of-medicine/)

## Paper primary topic

- [Peroxisome Proliferator-Activated Receptors](https://scholariq.org/topics/peroxisome-proliferator-activated-receptors/)

## Paper topics

- [Peroxisome Proliferator-Activated Receptors](https://scholariq.org/topics/peroxisome-proliferator-activated-receptors/)
- [Metabolism and Genetic Disorders](https://scholariq.org/topics/metabolism-and-genetic-disorders/)
- [Adipose Tissue and Metabolism](https://scholariq.org/topics/adipose-tissue-and-metabolism/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.