# Improved upper limb function in non-ambulant children with SMA type 2 and 3 during nusinersen treatment: a prospective 3-years SMArtCARE registry study

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/improved-upper-limb-function-in-non-ambulant-children-with-sma-type-2-and-3/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Astrid Pechmann,Max Behrens,Katharina Dörnbrack,Adrian Tassoni,Franziska Wenzel,Sabine Stein,Sibylle Emilie Vogt,Daniela Zöller,Günther Bernert,Tim Hagenacker,Ulrike Schara‐Schmidt,Maggie C. Walter,Astrid Bertsche,Katharina Vill,Matthias Baumann,Manuela Baumgärtner,Isabell Cordts,Astrid Eisenkölbl,Marina Flotats‐Bastardas,Johannes Friese,René Günther,Andreas Hahn,Veronka Horber,Ralf A. Husain,Sabine Illsinger,Jörg Jahnel,Jessika Johannsen,Cornelia Köhler,Heike Kölbel,Monika Müller,Arpad von Moers,Annette Schwerin-Nagel,Christof Reihle,Kurt Schlachter,Gudrun Schreiber,Oliver Schwartz,Martin Smitka,Elisabeth Steiner,Regina Trollmann,Markus Weiler,Claudia Weiß,Gert Wiegand,Ekkehard Wilichowski,Andreas Ziegler,Hanns Lochmüller,Janbernd Kirschner,SMArtCARE study group,Lisa Ameshofer,Bárbara Andres,Daniela Angelova-Toshkina,Daniela Banholzer,Christina Bant,Petra Baum,Sandra Baumann,Ute Baur,Benedikt Becker,Bettina Behring,Julia Bellut,Andrea Bevot,Jasmin Bischofberger,Lisa Bitzan,Bogdan Bjelica,Markus Blankenburg,Sandra Böger,Friederike Bonetti,Anke Bongartz,Svenja Brakemeier,Lisa Bratka,Nathalie Braun,Sarah Braun,Brigitte Brauner,Christa Bretschneider,Nadine Burgenmeister,Bea Burke,Sebahattin Çırak,Andrea Dall,Heike de Vries,Adela Della Marina,Jonas Denecke,Marcus Deschauer,Zylfie Dibrani,Uta Diebold,Lutz Dondit,Jessica Drebes,Joenna Driemeyer,Vladimir Dukic,Matthias Eckenweiler,Mirjam Eminger,Michal Fischer,Cornelia Fischer,Maren Freigang,Philippa Gaiser,Andrea Gangfuß,Stephanie Geitmann,Annette George,Magdalena Gosk-Tomek,Susanne Grinzinger,Kristina Gröning,Martin Groß,Anne‐Katrin Güttsches |
| Citations | 42 |
| DOI | 10.1186/s13023-022-02547-8 |
| Fields | Biochemistry, Genetics and Molecular Biology,Medicine |
| Open Access | true |
| OA Status | gold |
| OA URL | https://ojrd.biomedcentral.com/counter/pdf/10.1186/s13023-022-02547-8 |
| OpenAlex ID | https://openalex.org/W4307106827 |
| PMID | 36274155 |
| Type | article |
| Year | 2022 |

## Paper authors

- [Lars Hendrik Müschen](https://scholariq.org/researchers/lars-hendrik-muschen/)
- [Moritz Metelmann](https://scholariq.org/researchers/moritz-metelmann/)

## Paper journal

- [Orphanet Journal of Rare Diseases](https://scholariq.org/journals/orphanet-journal-of-rare-diseases/)

## Paper primary topic

- [Neurogenetic and Muscular Disorders Research](https://scholariq.org/topics/neurogenetic-and-muscular-disorders-research/)

## Paper topics

- [Neurogenetic and Muscular Disorders Research](https://scholariq.org/topics/neurogenetic-and-muscular-disorders-research/)
- [Spinal Dysraphism and Malformations](https://scholariq.org/topics/spinal-dysraphism-and-malformations/)
- [Craniofacial Disorders and Treatments](https://scholariq.org/topics/craniofacial-disorders-and-treatments/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.
