# Interim analyses of a first-in-human phase 1/2 mRNA trial for propionic acidaemia

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/interim-analyses-of-a-first-in-human-phase-1-2-mrna-trial-for-propionic/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Dwight D. Koeberl,Andreas Schulze,Neal Sondheimer,Gerald S. Lipshutz,Tarekegn Geberhiwot,Lerong Li,Rajnish Saini,Junxiang Luo,Vanja Sikirica,Ling Jin,M. Liang,Mary Leuchars,Stephanie Grünewald |
| Citations | 126 |
| DOI | 10.1038/s41586-024-07266-7 |
| Fields | Biochemistry, Genetics and Molecular Biology,Medicine |
| Open Access | true |
| OA Status | hybrid |
| OA URL | https://www.nature.com/articles/s41586-024-07266-7.pdf |
| OpenAlex ID | https://openalex.org/W4393870177 |
| PMID | 38570682 |
| Type | article |
| Year | 2024 |

## Paper authors

- [Vanja Sikirica](https://scholariq.org/researchers/vanja-sikirica/)

## Paper journal

- [Nature](https://scholariq.org/journals/nature/)

## Paper primary topic

- [Metabolism and Genetic Disorders](https://scholariq.org/topics/metabolism-and-genetic-disorders/)

## Paper topics

- [Metabolism and Genetic Disorders](https://scholariq.org/topics/metabolism-and-genetic-disorders/)
- [Folate and B Vitamins Research](https://scholariq.org/topics/folate-and-b-vitamins-research/)
- [Muscle metabolism and nutrition](https://scholariq.org/topics/muscle-metabolism-and-nutrition/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.
