# Long-Term Comparative Efficacy and Safety of Risdiplam versus Nusinersen in Children with Type 1 Spinal Muscular Atrophy (SMA)

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/long-term-comparative-efficacy-and-safety-of-risdiplam-versus-nusinersen-in/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Neil Hawkins,Gautam Sajeev,Rachel Evans,Anadi Mahajan,David A. Scott,Julian Nam,Chris Sutherland,Christos Kokaliaris |
| Citations | 0 |
| DOI | 10.1055/s-0043-1777162 |
| Fields | Biochemistry, Genetics and Molecular Biology,Medicine |
| Open Access | false |
| OA Status | closed |
| OpenAlex ID | https://openalex.org/W4416705610 |
| Type | article |
| Year | 2023 |

## Paper authors

- [Anadi Mahajan](https://scholariq.org/researchers/anadi-mahajan/)

## Paper journal

- [Neuropediatrics](https://scholariq.org/journals/neuropediatrics/)

## Paper primary topic

- [Neurogenetic and Muscular Disorders Research](https://scholariq.org/topics/neurogenetic-and-muscular-disorders-research/)

## Paper topics

- [Neurogenetic and Muscular Disorders Research](https://scholariq.org/topics/neurogenetic-and-muscular-disorders-research/)
- [Amyotrophic Lateral Sclerosis Research](https://scholariq.org/topics/amyotrophic-lateral-sclerosis-research/)
- [Muscle Physiology and Disorders](https://scholariq.org/topics/muscle-physiology-and-disorders/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.
