# Long-Term Effect of Gene Therapy on Leber’s Congenital Amaurosis

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/long-term-effect-of-gene-therapy-on-leber-s-congenital-amaurosis/

## Facts

| Field | Value |
| --- | --- |
| Author Names | James Bainbridge,Manjit Mehat,Venki Sundaram,Scott Robbie,Susie E. Barker,Caterina Ripamonti,Anastasios Georgiadis,Freya M. Mowat,Stuart G. Beattie,Peter J. Gardner,Kecia L. Feathers,Vy Luong,Suzanne Yzer,Kamaljit S. Balaggan,Ananth C. Viswanathan,Thomy de Ravel,Ingele Casteels,Graham E. Holder,Nick Tyler,Fred W. Fitzke,Richard G. Weleber,Marko Nardini,Anthony T. Moore,Debra A. Thompson,Simon M. Petersen‐Jones,Michel Michaelides,L. Ingeborgh van den Born,Andrew Stockman,Alexander J. Smith,Gary S. Rubin,Robin R. Ali |
| Citations | 744 |
| DOI | 10.1056/nejmoa1414221 |
| Fields | Biochemistry, Genetics and Molecular Biology |
| Open Access | true |
| OA Status | bronze |
| OA URL | https://www.nejm.org/doi/pdf/10.1056/NEJMoa1414221?articleTools=true |
| OpenAlex ID | https://openalex.org/W265142245 |
| PMID | 25938638 |
| Type | article |
| Year | 2015 |

## Paper authors

- [Michel Michaelides](https://scholariq.org/researchers/michel-michaelides/)

## Paper journal

- [New England Journal of Medicine](https://scholariq.org/journals/new-england-journal-of-medicine/)

## Paper primary topic

- [Retinal Development and Disorders](https://scholariq.org/topics/retinal-development-and-disorders/)

## Paper topics

- [Retinal Development and Disorders](https://scholariq.org/topics/retinal-development-and-disorders/)
- [Virus-based gene therapy research](https://scholariq.org/topics/virus-based-gene-therapy-research/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.