# Long-term follow-up of IPEX syndrome patients after different therapeutic strategies: An international multicenter retrospective study

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/long-term-follow-up-of-ipex-syndrome-patients-after-different-therapeutic/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Federica Barzaghi,Laura Cristina Amaya Hernandez,Bénédicte Neven,Silvia Ricci,Zeynep Yesim Kucuk,Jack Bleesing,Zohreh Nademi,Mary Slatter,Erlinda R. Ulloa,Anna Shcherbina,Anna Roppelt,Austen Worth,Juliana Silva,Alessandro Aiuti,Luis Murguía-Favela,Carsten Speckmann,Magda Carneiro‐Sampaio,Juliana Folloni Fernandes,Safa Barış,Ahmet Özen,Elif Karakoç-Aydıner,Ayça Kıykım,Ansgar Schulz,Sandra Steinmann,Lucia Dora Notarangelo,Eleonora Gambineri,Paolo Lionetti,William T. Shearer,Lisa R. Forbes,Caridad Martinez,Despina Moshous,Stéphane Blanche,Alain Fisher,Frank M. Ruemmele,Côme Tissandier,O Marie,Frédéric Rieux‐Laucat,Marina Cavazzana,Waseem Qasim,Barbarella Lucarelli,Michael H. Albert,Ichiro Kobayashi,Laura Alonso,Cristina Díaz de Heredia,Hirokazu Kanegane,Ánita Lawitschka,Jong Jin Seo,Marta González‐Vicent,Miguel Ángel Díaz,Rakesh K. Goyal,Martin G. Sauer,Akif Yeşilipek,Min‐Soo Kim,Yeşim Yılmaz Demirdağ,Monica Bhatia,Julie Khlevner,Erick J. Richmond Padilla,Silvana Martino,Davide Montin,Olaf Neth,Águeda Molinos-Quintana,Justo Valverde-Fernández,Arnon Broides,Vered Pinsk,Antje Ballauf,Filomeen Haerynck,Victoria Bordon,Catharina Dhooge,Maria Garcia-Lloret,Robbert G. M. Bredius,Krzysztof Kałwak,Élie Haddad,Markus G. Seidel,Gregor Dückers,Sung‐Yun Pai,Christopher C. Dvorak,Stephan Ehl,Franco Locatelli,Frederick D. Goldman,Andrew R. Gennery,Mort J. Cowan,Maria-Grazia Roncarolo,Rosa Bacchetta |
| Citations | 318 |
| DOI | 10.1016/j.jaci.2017.10.041 |
| Fields | Immunology and Microbiology,Medicine |
| Open Access | true |
| OA Status | hybrid |
| OA URL | http://www.jacionline.org/article/S0091674917318936/pdf |
| OpenAlex ID | https://openalex.org/W2774825032 |
| PMID | 29241729 |
| Type | article |
| Year | 2017 |

## Paper authors

- [Ansgar Schulz](https://scholariq.org/researchers/ansgar-schulz/)

## Paper journal

- [Journal of Allergy and Clinical Immunology](https://scholariq.org/journals/journal-of-allergy-and-clinical-immunology/)

## Paper primary topic

- [Adrenal Hormones and Disorders](https://scholariq.org/topics/adrenal-hormones-and-disorders/)

## Paper topics

- [Adrenal Hormones and Disorders](https://scholariq.org/topics/adrenal-hormones-and-disorders/)
- [T-cell and B-cell Immunology](https://scholariq.org/topics/t-cell-and-b-cell-immunology/)
- [Immunodeficiency and Autoimmune Disorders](https://scholariq.org/topics/immunodeficiency-and-autoimmune-disorders/)

---
Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.
