# Long-Term Tofersen in <i>SOD1</i> Amyotrophic Lateral Sclerosis

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/long-term-tofersen-in-i-sod1-i-amyotrophic-lateral-sclerosis/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Timothy M. Miller,Merit Cudkowicz,Pamela Shaw,Angela Genge,Gen Sobue,Robert C. Bucelli,Adriano Chiò,Philip Van Damme,Albert C. Ludolph,Jonathan D. Glass,Jinsy Andrews,Suma Babu,Michael Benatar,C. McDermott,François Salachas,Gaëlle Bruneteau,Ammar Al-Chalabi,Matthew Amorin,Ivan Nestorov,Danielle Graham,Luan Lin,Peng Sun,Manjit McNeill,Sohail Malek,Jennifer Inra,Steve Garafalo,Stephanie Fradette,VALOR and OLE Working Group,Lien Beullens,Kristl Claeys,Thomas Claeys,Goedele Couwelier,Ann D'Hondt,Elisa Debien,Sebastiaan De Keersmaecker,Laetitia della Faille,Koen Delmotte,Sofie DR Depoortere,Laura de Velder,Laurens Dobbels,Jeroen Gijs,Simon Horckmans,Nikita Lamaire,Hannelore Liessens,Pegah Masrori,Céline Nysten,Caroline Schotte,Anouk Serrien,Bart Swinnen,Petra Tilkin,Sien Hilde Van Daele,Van Damme Pa,Jan Vynckier,Anke Wouters,Agessandro Abrahão,Mark Angle,Mohamed Badawy,Maxime Berube,Vanessa Bertone,Sarah Marie Cooper,Peter Dobrowolski,Helen Fong,Angela Genge,Matthew Hannouche,Denise Hartley,Michael Hogan,Wendy Johnston,Yousra Khalfallah,Lawrence Korngut,Gina Kroetsch,Justin Létourneau,Claire Magnussen,José Corberá Martínez,Rami Massie,Theodore Mobach,Jahan Mookshah,Timur Özelsel,Andrea Parks,Janet Petrillo,Gerald Pfeffer,Shirley Pham,Liane Phung,Rodney Shiungsun,Li Pi-Shan,Denizart Santos,Kristiana Salmon,Natalie Saunders,Dylan Sembinelli,Kelsey Tymkow,Berchman Wong,Lorne Zinman,Merete Karlsborg,Therese Pedersen Lomholt,Sigrid Nilsson,Lisette Salvesen,P. Stahl Skov,Kristen Svenstrup,Gaëlle Bruneteau,Frederic Clarencon,Raquel Guimarães Costa |
| Citations | 20 |
| DOI | 10.1001/jamaneurol.2025.4946 |
| Fields | Medicine,Neuroscience |
| Open Access | true |
| OA Status | hybrid |
| OA URL | https://jamanetwork.com/journals/jamaneurology/articlepdf/2843130/jamaneurology_miller_2025_oi_250084_1769188938.09478.pdf |
| OpenAlex ID | https://openalex.org/W7117237225 |
| PMID | 41661214 |
| Type | article |
| Year | 2026 |

## Paper authors

- [Adèle Hesters](https://scholariq.org/researchers/adele-hesters/)

## Paper journal

- [JAMA Neurology](https://scholariq.org/journals/jama-neurology/)

## Paper primary topic

- [Amyotrophic Lateral Sclerosis Research](https://scholariq.org/topics/amyotrophic-lateral-sclerosis-research/)

## Paper topics

- [Amyotrophic Lateral Sclerosis Research](https://scholariq.org/topics/amyotrophic-lateral-sclerosis-research/)
- [Genetic Neurodegenerative Diseases](https://scholariq.org/topics/genetic-neurodegenerative-diseases/)
- [Neurogenetic and Muscular Disorders Research](https://scholariq.org/topics/neurogenetic-and-muscular-disorders-research/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.
