# Lumasiran, an RNAi Therapeutic for Primary Hyperoxaluria Type 1

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/lumasiran-an-rnai-therapeutic-for-primary-hyperoxaluria-type-1/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Sander F. Garrelfs,Yaacov Frishberg,Sally A. Hulton,Michael J. Koren,William O’Riordan,Pierre Cochat,Georges Deschênes,Hadas Shasha‐Lavsky,Jeffrey M. Saland,William G. van’t Hoff,Daniel G. Fuster,Daniella Magen,Shabbir H. Moochhala,Gesa Schalk,Eva Šimková,Jaap W. Groothoff,David J. Sas,Kristin Meliambro,Jiandong Lu,Marianne T. Sweetser,Pushkal Garg,Akshay Vaishnaw,John M. Gansner,Tracy L. McGregor,John C. Lieske |
| Citations | 507 |
| DOI | 10.1056/nejmoa2021712 |
| Fields | Medicine |
| Open Access | true |
| OA Status | bronze |
| OA URL | https://www.nejm.org/doi/pdf/10.1056/NEJMoa2021712?articleTools=true |
| OpenAlex ID | https://openalex.org/W3151149834 |
| PMID | 33789010 |
| Type | article |
| Year | 2021 |

## Paper authors

- [Kristin Meliambro](https://scholariq.org/researchers/kristin-meliambro/)
- [John C. Lieske](https://scholariq.org/researchers/john-c-lieske/)

## Paper journal

- [New England Journal of Medicine](https://scholariq.org/journals/new-england-journal-of-medicine/)

## Paper primary topic

- [Kidney Stones and Urolithiasis Treatments](https://scholariq.org/topics/kidney-stones-and-urolithiasis-treatments/)

## Paper topics

- [Kidney Stones and Urolithiasis Treatments](https://scholariq.org/topics/kidney-stones-and-urolithiasis-treatments/)
- [Biomedical Research and Pathophysiology](https://scholariq.org/topics/biomedical-research-and-pathophysiology/)
- [Chemotherapy-induced organ toxicity mitigation](https://scholariq.org/topics/chemotherapy-induced-organ-toxicity-mitigation/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.
