# Management goals for type 1 Gaucher disease: An expert consensus document from the European working group on Gaucher disease

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/management-goals-for-type-1-gaucher-disease-an-expert-consensus-document-from/

## Facts

| Field | Value |
| --- | --- |
| Author Names | M. Biegstraaten,Timothy M. Cox,Nadia Belmatoug,Marc Berger,Tanya Collin-Histed,Stephan vom Dahl,M. Di Rocco,Cristina Fraga,Fiorina Giona,Pilar Giraldo,Mensuda Hasanhodžić,Derralynn Hughes,Per Ole Iversen,Aline Kiewiet,Elena Lukina,Maciej Machaczka,Theodore Marinakis,Eugen Mengel,Gregory M. Pastores,Ursula Plöckinger,Hanna Rosenbaum,J. Serratrice,Argiris Symeonidis,Jeff Szer,J. Timmerman,Anna Tylki‐Szymańska,Monika Weisz Hubshman,Dimitrios Zafeiriou,Ari Zimran,Carla E. M. Hollak |
| Citations | 136 |
| DOI | 10.1016/j.bcmd.2016.10.008 |
| Fields | Biochemistry, Genetics and Molecular Biology,Medicine |
| Open Access | true |
| OA Status | hybrid |
| OA URL | https://www.sciencedirect.com/science/article/pii/S1079979616301917/pdf |
| OpenAlex ID | https://openalex.org/W2533008867 |
| PMID | 28274788 |
| Type | article |
| Year | 2016 |

## Paper authors

- [Per Ole Iversen](https://scholariq.org/researchers/per-ole-iversen/)

## Paper primary topic

- [Lysosomal Storage Disorders Research](https://scholariq.org/topics/lysosomal-storage-disorders-research/)

## Paper topics

- [Lysosomal Storage Disorders Research](https://scholariq.org/topics/lysosomal-storage-disorders-research/)
- [Studies on Chitinases and Chitosanases](https://scholariq.org/topics/studies-on-chitinases-and-chitosanases/)
- [Trypanosoma species research and implications](https://scholariq.org/topics/trypanosoma-species-research-and-implications/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.
