# Mitapivat in adults with non-transfusion-dependent α-thalassaemia or β-thalassaemia (ENERGIZE): a phase 3, international, randomised, double-blind, placebo-controlled trial

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/mitapivat-in-adults-with-non-transfusion-dependent-thalassaemia-or-thalassaemia/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Alì Taher,Ali T Taher,Hanny Al‐Samkari,Yeşim Aydınok,Martin Besser,Audra Boscoe,Jayme L. Dahlin,Gonzalo De Luna,Jeremie H. Estepp,Sarah Gheuens,Keely Gilroy,Andreas Glenthøj,Ai Sim Goh,Varsha Iyer,Antonis Kattamis,Sandra Regina Loggetto,Susan Morris,Khaled M. Musallam,Kareem Osman,Paolo Ricchi,Eduardo Salido-Fiérrez,Sujit Sheth,Feng Tai,Heather Tevich,Katrin Uhlig,Rolandas Urbstonaitis,Vip Viprakasit,Maria Domenica Cappellini,Kevin H M Kuo,Sandra Fatima Menosi Gualandro,Guilherme Henrique Hencklain Fonseca,Karina Tozatto Maio,Liliana Mitie Suganuma,Luan Lima Marchi,Rebeca Cavalcanti Galle de Aguiar,Vitor Mauad,Marcelo Rodrigues Bacci,Ana Silva Pinto,Jõao Henrique Nogueira,Luciana Maria Mendes Santiago,Victor Emanuel Fernandes da Costa,Sandra Regina Loggetto,Renato Cerqueira de Souza,Sérgio Domingos Vieira,Lucas Tramujas,Guilherme Rasia Bosi,Fábio Eduardo Camazzola,Viviani de Lourdes Rosa Pessoa,Bruna Froede Neumann,Julia Carrara Vieira,Desislava Ilieva-Chiviyska,Nina Krasteva,Lachezar Bogdanov,Silvia Naneva,Penka Ganeva,Mirella Rangelova,Viktoria Yankova,Mariya Todorova,Maria Jukova,Pencho Georgiev,Byulent Nihat,Zhanet Grudeva-Popova,Kevin Kuo,Andrew Binding,Christopher Patriquin,Jacob Pendergrast,Jameel Abdulrehman,Joanna Loh,John Aneke,Richard Ward,Andreas Glenthøj,Nina Toft,Sarah Birgitte Ingemod Sand Carlsen,Pablo Bartolucci,Amna Jebali,Anoosha Habibi,Clara Noizat,Gonzalo De Luna,Fatima Bensiradj,Jamila Alhamrouni,Suella Martino,Giovanna Cannas,Manon Marie,Emilie Virot,Ferras Alashkar,Alexander Röth,Antonis Kattamis,Elena Chatzikalil,Georgia Perissaki,Konstantina Toutoudaki,Maria Moraki,Maria-Ionna Chatzieleftheriou,Polyxeni Delaporta,Vasiliki Chouliara,Alexandra Kourakli-Symeonidis,Anargyros Symeonidis,Maria-Lamprini Kasti,Vasileios Lazaris,Vasiliki Lampropoulou,Efthymia Vlachaki |
| Citations | 15 |
| DOI | 10.1016/s0140-6736(25)00635-x |
| Fields | Medicine |
| Open Access | true |
| OA Status | green |
| OA URL | https://hdl.handle.net/11380/1410168 |
| OpenAlex ID | https://openalex.org/W4411439465 |
| PMID | 40544857 |
| Type | article |
| Year | 2025 |

## Paper authors

- [Kareem Osman](https://scholariq.org/researchers/kareem-osman/)

## Paper journal

- [The Lancet](https://scholariq.org/journals/the-lancet/)

## Paper primary topic

- [Hemoglobinopathies and Related Disorders](https://scholariq.org/topics/hemoglobinopathies-and-related-disorders/)

## Paper topics

- [Hemoglobinopathies and Related Disorders](https://scholariq.org/topics/hemoglobinopathies-and-related-disorders/)
- [Blood transfusion and management](https://scholariq.org/topics/blood-transfusion-and-management/)
- [Erythropoietin and Anemia Treatment](https://scholariq.org/topics/erythropoietin-and-anemia-treatment/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.
