# Nusinersen initiated in infants during the presymptomatic stage of spinal muscular atrophy: Interim efficacy and safety results from the Phase 2 NURTURE study

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/nusinersen-initiated-in-infants-during-the-presymptomatic-stage-of-spinal/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Darryl C. De Vivo,Enrico Bertini,Kathryn J. Swoboda,Wuh‐Liang Hwu,Thomas O. Crawford,Richard S. Finkel,Janbernd Kirschner,Nancy L. Kuntz,Julie Parsons,Monique M. Ryan,Russell J. Butterfield,Haluk Topaloğlu,Tawfeg Ben‐Omran,Valeria Sansone,Yuh‐Jyh Jong,Francy Shu,John F. Staropoli,Douglas A. Kerr,Alfred Sandrock,Christopher Stebbins,Marco Petrillo,Gabriel Braley,Kristina Johnson,Richard Foster,Sarah Gheuens,Ishir Bhan,Sandra P. Reyna,Stephanie Fradette,Wildon Farwell |
| Citations | 633 |
| DOI | 10.1016/j.nmd.2019.09.007 |
| Fields | Medicine |
| Open Access | true |
| OA Status | hybrid |
| OA URL | http://www.nmd-journal.com/article/S0960896619311277/pdf |
| OpenAlex ID | https://openalex.org/W2972356268 |
| PMID | 31704158 |
| Type | article |
| Year | 2019 |

## Paper authors

- [Janbernd Kirschner](https://scholariq.org/researchers/janbernd-kirschner/)

## Paper primary topic

- [Neurogenetic and Muscular Disorders Research](https://scholariq.org/topics/neurogenetic-and-muscular-disorders-research/)

## Paper topics

- [Neurogenetic and Muscular Disorders Research](https://scholariq.org/topics/neurogenetic-and-muscular-disorders-research/)
- [Congenital Anomalies and Fetal Surgery](https://scholariq.org/topics/congenital-anomalies-and-fetal-surgery/)
- [Cardiac Structural Anomalies and Repair](https://scholariq.org/topics/cardiac-structural-anomalies-and-repair/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.