# Nusinersen versus Sham Control in Later-Onset Spinal Muscular Atrophy

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/nusinersen-versus-sham-control-in-later-onset-spinal-muscular-atrophy/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Eugenio Mercuri,Basil T. Darras,Claudia A. Chiriboga,John W. Day,Craig Campbell,Anne M. Connolly,Susan T. Iannaccone,Janbernd Kirschner,Nancy L. Kuntz,Kayoko Saito,Perry B. Shieh,M. Tulinius,Elena Mazzone,Jacqueline Montes,Kathie M. Bishop,Qingqing Yang,Richard Foster,Sarah Gheuens,C. Frank Bennett,Wildon Farwell,Eugene Schneider,Darryl C. De Vivo,Richard S. Finkel |
| Citations | 1,443 |
| DOI | 10.1056/nejmoa1710504 |
| Fields | Biochemistry, Genetics and Molecular Biology,Medicine |
| Open Access | true |
| OA Status | green |
| OA URL | https://digitalcommons.wustl.edu/cgi/viewcontent.cgi?article=7557&context=open_access_pubs |
| OpenAlex ID | https://openalex.org/W2789114047 |
| PMID | 29443664 |
| Type | article |
| Year | 2018 |

## Paper authors

- [Janbernd Kirschner](https://scholariq.org/researchers/janbernd-kirschner/)

## Paper journal

- [New England Journal of Medicine](https://scholariq.org/journals/new-england-journal-of-medicine/)

## Paper primary topic

- [Neurogenetic and Muscular Disorders Research](https://scholariq.org/topics/neurogenetic-and-muscular-disorders-research/)

## Paper topics

- [Neurogenetic and Muscular Disorders Research](https://scholariq.org/topics/neurogenetic-and-muscular-disorders-research/)
- [Amyotrophic Lateral Sclerosis Research](https://scholariq.org/topics/amyotrophic-lateral-sclerosis-research/)
- [Muscle Physiology and Disorders](https://scholariq.org/topics/muscle-physiology-and-disorders/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.
