# Onasemnogene abeparvovec for presymptomatic infants with three copies of SMN2 at risk for spinal muscular atrophy: the Phase III SPR1NT trial

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/onasemnogene-abeparvovec-for-presymptomatic-infants-with-three-copies-of-smn2-at/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Kevin A. Strauss,Michelle A. Farrar,Francesco Muntoni,Kayoko Saito,Jerry R. Mendell,Laurent Servais,Hugh J. McMillan,Richard S. Finkel,Kathryn J. Swoboda,Jennifer M. Kwon,Craig M. Zaidman,Claudia A. Chiriboga,Susan T. Iannaccone,Jena M. Krueger,Julie Parsons,Perry B. Shieh,Sarah Kavanagh,Melissa Wigderson,Sitra Tauscher‐Wisniewski,Bryan E. McGill,Thomas A. Macek |
| Citations | 282 |
| DOI | 10.1038/s41591-022-01867-3 |
| Fields | Biochemistry, Genetics and Molecular Biology,Medicine |
| Open Access | true |
| OA Status | hybrid |
| OA URL | https://www.nature.com/articles/s41591-022-01867-3.pdf |
| OpenAlex ID | https://openalex.org/W4283031673 |
| PMID | 35715567 |
| Type | article |
| Year | 2022 |

## Paper authors

- [Hugh J. McMillan](https://scholariq.org/researchers/hugh-j-mcmillan/)

## Paper journal

- [Nature Medicine](https://scholariq.org/journals/nature-medicine/)

## Paper primary topic

- [Neurogenetic and Muscular Disorders Research](https://scholariq.org/topics/neurogenetic-and-muscular-disorders-research/)

## Paper topics

- [Neurogenetic and Muscular Disorders Research](https://scholariq.org/topics/neurogenetic-and-muscular-disorders-research/)
- [Congenital Anomalies and Fetal Surgery](https://scholariq.org/topics/congenital-anomalies-and-fetal-surgery/)
- [RNA modifications and cancer](https://scholariq.org/topics/rna-modifications-and-cancer/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.