# Onasemnogene abeparvovec for presymptomatic infants with two copies of SMN2 at risk for spinal muscular atrophy type 1: the Phase III SPR1NT trial

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/onasemnogene-abeparvovec-for-presymptomatic-infants-with-two-copies-of-smn2-at/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Kevin A. Strauss,Michelle A. Farrar,Francesco Muntoni,Kayoko Saito,Jerry R. Mendell,Laurent Servais,Hugh J. McMillan,Richard S. Finkel,Kathryn J. Swoboda,Jennifer M. Kwon,Craig M. Zaidman,Claudia A. Chiriboga,Susan T. Iannaccone,Jena M. Krueger,Julie Parsons,Perry B. Shieh,Sarah Kavanagh,Sitra Tauscher‐Wisniewski,Bryan E. McGill,Thomas A. Macek |
| Citations | 304 |
| DOI | 10.1038/s41591-022-01866-4 |
| Fields | Biochemistry, Genetics and Molecular Biology,Medicine |
| Open Access | true |
| OA Status | hybrid |
| OA URL | https://www.nature.com/articles/s41591-022-01866-4.pdf |
| OpenAlex ID | https://openalex.org/W4283011798 |
| PMID | 35715566 |
| Type | article |
| Year | 2022 |

## Paper authors

- [Hugh J. McMillan](https://scholariq.org/researchers/hugh-j-mcmillan/)

## Paper journal

- [Nature Medicine](https://scholariq.org/journals/nature-medicine/)

## Paper primary topic

- [Neurogenetic and Muscular Disorders Research](https://scholariq.org/topics/neurogenetic-and-muscular-disorders-research/)

## Paper topics

- [Neurogenetic and Muscular Disorders Research](https://scholariq.org/topics/neurogenetic-and-muscular-disorders-research/)
- [RNA modifications and cancer](https://scholariq.org/topics/rna-modifications-and-cancer/)
- [Congenital Anomalies and Fetal Surgery](https://scholariq.org/topics/congenital-anomalies-and-fetal-surgery/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.