# Oral pharmacological chaperone migalastat compared with enzyme replacement therapy in Fabry disease: 18-month results from the randomised phase III ATTRACT study

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/oral-pharmacological-chaperone-migalastat-compared-with-enzyme-replacement/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Derralynn Hughes,Kathy Nicholls,Suma P. Shankar,Gere Sunder–Plassmann,David M. Koeller,Khan Nedd,Gerard Vockley,Takashi Hamazaki,Robin Lachmann,Toya Ohashi,Iacopo Olivotto,Norio Sakai,Patrick Deegan,David Dimmock,François Eyskens,Dominique P. Germain,Özlem Göker-Alpan,É. Hachulla,Ana Jovanović,Charles Marques Lourenço,Ichiei Narita,Mark Thomas,William R. Wilcox,Daniel G. Bichet,Raphael Schiffmann,Elizabeth Ludington,Christopher Viereck,John Kirk,Julie Yu,Franklin K. Johnson,Pol Boudes,Elfrida R. Benjamin,David J. Lockhart,Carrolee Barlow,Nina Skuban,Jeffrey P. Castelli,Jay Barth,Ulla Feldt‐Rasmussen |
| Citations | 390 |
| DOI | 10.1136/jmedgenet-2016-104178 |
| Fields | Medicine |
| Open Access | true |
| OA Status | hybrid |
| OA URL | https://jmg.bmj.com/content/jmedgenet/54/4/288.full.pdf |
| OpenAlex ID | https://openalex.org/W2551668015 |
| PMID | 27834756 |
| Type | article |
| Year | 2016 |

## Paper authors

- [Ichiei Narita](https://scholariq.org/researchers/ichiei-narita/)
- [Daniel G. Bichet](https://scholariq.org/researchers/daniel-g-bichet/)

## Paper primary topic

- [Lysosomal Storage Disorders Research](https://scholariq.org/topics/lysosomal-storage-disorders-research/)

## Paper topics

- [Lysosomal Storage Disorders Research](https://scholariq.org/topics/lysosomal-storage-disorders-research/)
- [Biomedical Research and Pathophysiology](https://scholariq.org/topics/biomedical-research-and-pathophysiology/)
- [Glycogen Storage Diseases and Myoclonus](https://scholariq.org/topics/glycogen-storage-diseases-and-myoclonus/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.