# P08 Long-term comparative efficacy and safety of risdiplam versus nusinersen in children with Type 1 spinal muscular atrophy (SMA)

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/p08-long-term-comparative-efficacy-and-safety-of-risdiplam-versus-nusinersen-in/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Gautam Sajeev,Rachel Evans,Neil Hawkins,Anadi Mahajan,David A. Scott,J. Nam,S.S. Sutherland,Christos Kokaliaris |
| Citations | 2 |
| DOI | 10.1016/j.nmd.2023.07.385 |
| Fields | Medicine |
| Open Access | false |
| OA Status | closed |
| OpenAlex ID | https://openalex.org/W4387307249 |
| Type | conference-abstract |
| Year | 2023 |

## Paper authors

- [Anadi Mahajan](https://scholariq.org/researchers/anadi-mahajan/)

## Paper primary topic

- [Neurogenetic and Muscular Disorders Research](https://scholariq.org/topics/neurogenetic-and-muscular-disorders-research/)

## Paper topics

- [Neurogenetic and Muscular Disorders Research](https://scholariq.org/topics/neurogenetic-and-muscular-disorders-research/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.
