# Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/patisiran-an-rnai-therapeutic-for-hereditary-transthyretin-amyloidosis/

## Facts

| Field | Value |
| --- | --- |
| Author Names | David Adams,Alejandra González‐Duarte,William O’Riordan,Chih‐Chao Yang,Mitsuharu Ueda,Arnt V. Kristen,Ivailo Tournev,Hartmut Schmidt,Teresa Coelho,John L. Berk,Kon-Ping Lin,Giuseppe Vita,Shahram Attarian,Violaine Planté‐Bordeneuve,Michelle M. Mezei,Josep M. Campistol,Juan Buades,Thomas H. Brannagan,Byoung J. Kim,Jeeyoung Oh,Yeşim Parman,Yoshiki Sekijima,Philip N. Hawkins,Scott D. Solomon,Michael Polydefkis,P. James B. Dyck,Pritesh J. Gandhi,Sunita Goyal,Jihong Chen,Andrew Strahs,Saraswathy V. Nochur,Marianne T. Sweetser,Pushkal Garg,Akshay Vaishnaw,Jared Gollob,Ole B. Suhr |
| Citations | 2,975 |
| DOI | 10.1056/nejmoa1716153 |
| Fields | Biochemistry, Genetics and Molecular Biology,Medicine |
| Open Access | true |
| OA Status | bronze |
| OA URL | https://www.nejm.org/doi/pdf/10.1056/NEJMoa1716153?articleTools=true |
| OpenAlex ID | https://openalex.org/W2810909862 |
| PMID | 29972753 |
| Type | article |
| Year | 2018 |

## Paper authors

- [Scott D. Solomon](https://scholariq.org/researchers/scott-d-solomon/)

## Paper journal

- [New England Journal of Medicine](https://scholariq.org/journals/new-england-journal-of-medicine/)

## Paper primary topic

- [Amyloidosis: Diagnosis, Treatment, Outcomes](https://scholariq.org/topics/amyloidosis-diagnosis-treatment-outcomes/)

## Paper topics

- [Amyloidosis: Diagnosis, Treatment, Outcomes](https://scholariq.org/topics/amyloidosis-diagnosis-treatment-outcomes/)
- [Alzheimer's disease research and treatments](https://scholariq.org/topics/alzheimer-s-disease-research-and-treatments/)
- [Skin and Cellular Biology Research](https://scholariq.org/topics/skin-and-cellular-biology-research/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.
