# Phase 1–2 Trial of Antisense Oligonucleotide Tofersen for <i>SOD1</i> ALS

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/phase-1-2-trial-of-antisense-oligonucleotide-tofersen-for-i-sod1-i-als/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Jonathan Mill,Merit Cudkowicz,Pamela J. Shaw,Peter M. Andersen,Nazem Atassi,Robert C. Bucelli,Angela Genge,Jonathan D. Glass,Shafeeq Ladha,Albert Ludolph,Nicholas J. Maragakis,Christopher McDermott,Alan Pestronk,John Ravits,François Salachas,Randall Trudell,Philip Van Damme,Lorne Zinman,C. Frank Bennett,Roger Lane,Alfred Sandrock,Heiko Runz,Danielle Graham,Hani Houshyar,Alexander McCampbell,Ivan Nestorov,Ih Chang,Manjit McNeill,Laura Fanning,Stephanie Fradette,Toby A. Ferguson |
| Citations | 556 |
| DOI | 10.1056/nejmoa2003715 |
| Fields | Medicine,Neuroscience |
| Open Access | true |
| OA Status | bronze |
| OA URL | https://www.nejm.org/doi/pdf/10.1056/NEJMoa2003715?articleTools=true |
| OpenAlex ID | https://openalex.org/W3040840440 |
| PMID | 32640130 |
| Type | article |
| Year | 2020 |

## Paper authors

- [François Salachas](https://scholariq.org/researchers/francois-salachas-2/)

## Paper journal

- [New England Journal of Medicine](https://scholariq.org/journals/new-england-journal-of-medicine/)

## Paper primary topic

- [Amyotrophic Lateral Sclerosis Research](https://scholariq.org/topics/amyotrophic-lateral-sclerosis-research/)

## Paper topics

- [Amyotrophic Lateral Sclerosis Research](https://scholariq.org/topics/amyotrophic-lateral-sclerosis-research/)
- [Genetic Neurodegenerative Diseases](https://scholariq.org/topics/genetic-neurodegenerative-diseases/)
- [Tuberous Sclerosis Complex Research](https://scholariq.org/topics/tuberous-sclerosis-complex-research/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.