# Preclinical modeling highlights the therapeutic potential of hematopoietic stem cell gene editing for correction of SCID-X1

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/preclinical-modeling-highlights-the-therapeutic-potential-of-hematopoietic-stem/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Giulia Schiroli,Samuele Ferrari,Anthony Conway,Aurélien Jacob,Valentina Capo,Luisa Albano,Tiziana Plati,Maria Carmina Castiello,Francesca Sanvito,Andrew R. Gennery,Chiara Bovolenta,Rahul Palchaudhuri,David T. Scadden,Michael C. Holmes,Anna Villa,Giovanni Sitia,Angelo Lombardo,Pietro Genovese,Luigi Naldini |
| Citations | 217 |
| DOI | 10.1126/scitranslmed.aan0820 |
| Fields | Biochemistry, Genetics and Molecular Biology,Medicine |
| Open Access | false |
| OA Status | closed |
| OpenAlex ID | https://openalex.org/W2761956671 |
| PMID | 29021165 |
| Type | article |
| Year | 2017 |

## Paper authors

- [Valentina Capo](https://scholariq.org/researchers/valentina-capo/)
- [Anna Villa](https://scholariq.org/researchers/anna-villa/)

## Paper primary topic

- [CRISPR and Genetic Engineering](https://scholariq.org/topics/crispr-and-genetic-engineering/)

## Paper topics

- [CRISPR and Genetic Engineering](https://scholariq.org/topics/crispr-and-genetic-engineering/)
- [Virus-based gene therapy research](https://scholariq.org/topics/virus-based-gene-therapy-research/)
- [CAR-T cell therapy research](https://scholariq.org/topics/car-t-cell-therapy-research/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.