# Safety and efficacy of low-dose sirolimus in the PIK3CA-related overgrowth spectrum

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/safety-and-efficacy-of-low-dose-sirolimus-in-the-pik3ca-related-overgrowth/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Victoria Parker,Kim M. Keppler‐Noreuil,Laurence Faivre,Maxime Luu,Neal L. Oden,Leena De Silva,Julie C. Sapp,Katrina Andrews,Marc Bardou,Kong Y. Chen,Thomas N. Darling,Élodie Gautier,Barry R. Goldspiel,S. Hadj‐Rabia,Julie Harris,Georgios Kounidas,Parag Kumar,Marjorie J. Lindhurst,Romaric Loffroy,Ludovic Martin,Alice Phan,Kristina I. Rother,Brigitte C. Widemann,Pamela L. Wolters,Christine Coubes,Lucile Pinson,Marjolaine Willems,Catherine Vincent‐Delorme,P. Vabres,Robert K. Semple,Leslie G. Biesecker |
| Citations | 158 |
| DOI | 10.1038/s41436-018-0297-9 |
| Fields | Biochemistry, Genetics and Molecular Biology |
| Open Access | true |
| OA Status | hybrid |
| OA URL | https://www.gimjournal.org/article/S1098-3600(21)01473-8/pdf |
| OpenAlex ID | https://openalex.org/W2892878289 |
| PMID | 30270358 |
| Type | article |
| Year | 2018 |

## Paper authors

- [Pamela L. Wolters](https://scholariq.org/researchers/pamela-l-wolters/)
- [Brigitte C. Widemann](https://scholariq.org/researchers/brigitte-c-widemann/)

## Paper primary topic

- [PI3K/AKT/mTOR signaling in cancer](https://scholariq.org/topics/pi3k-akt-mtor-signaling-in-cancer/)

## Paper topics

- [PI3K/AKT/mTOR signaling in cancer](https://scholariq.org/topics/pi3k-akt-mtor-signaling-in-cancer/)
- [Genetic Syndromes and Imprinting](https://scholariq.org/topics/genetic-syndromes-and-imprinting/)
- [Muscle Physiology and Disorders](https://scholariq.org/topics/muscle-physiology-and-disorders/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.
