# Successful engraftment of gene-corrected hematopoietic stem cells in non-conditioned patients with Fanconi anemia

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/successful-engraftment-of-gene-corrected-hematopoietic-stem-cells-in-non/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Paula Rı́o,Susana Navarro,Wei Wang,Rebeca Sánchez‐Domínguez,Roser Pujol,José C. Segovia,Massimo Bogliolo,Eva Merino,Ning Wu,Rocío Salgado,María L. Lamana,Rosa María Pérez Yáñez,José Antonio Casado,Yari Giménez,Francisco J Roman‐Rodriguez,Lara Álvarez,Omaira Alberquilla,Anna Raimbault,Guillermo Güenechea,M. Luz Lozano,Laura Cerrato,Miriam Hernando-Rodríguez,Eva Heredero Gálvez,Raquel Hladun,Irina Giralt,Jordi Barquinero,Anne Galy,Nagore García de Andoín,Ricardo López Almaraz,Albert Català,Jonathan D. Schwartz,Jordi Surrallés,Jean Soulier,Manfred Schmidt,Cristina Díaz de Heredia,Julián Sevilla,Juan A. Bueren |
| Citations | 179 |
| DOI | 10.1038/s41591-019-0550-z |
| Fields | Biochemistry, Genetics and Molecular Biology,Neuroscience |
| Open Access | false |
| OA Status | closed |
| OpenAlex ID | https://openalex.org/W2972171376 |
| PMID | 31501599 |
| Type | article |
| Year | 2019 |

## Paper authors

- [Jonathan D. Schwartz](https://scholariq.org/researchers/jonathan-d-schwartz/)

## Paper journal

- [Nature Medicine](https://scholariq.org/journals/nature-medicine/)

## Paper primary topic

- [DNA Repair Mechanisms](https://scholariq.org/topics/dna-repair-mechanisms/)

## Paper topics

- [DNA Repair Mechanisms](https://scholariq.org/topics/dna-repair-mechanisms/)
- [CRISPR and Genetic Engineering](https://scholariq.org/topics/crispr-and-genetic-engineering/)
- [Genetic Neurodegenerative Diseases](https://scholariq.org/topics/genetic-neurodegenerative-diseases/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.
