# Treatment of a metabolic liver disease by in vivo genome base editing in adult mice

**Type:** Papers  
**Canonical URL:** https://scholariq.org/papers/treatment-of-a-metabolic-liver-disease-by-in-vivo-genome-base-editing-in-adult/

## Facts

| Field | Value |
| --- | --- |
| Author Names | Lukas Villiger,Hiu Man Grisch‐Chan,Helen Lindsay,Femke Ringnalda,Chiara Balbo Pogliano,Gabriella Allegri,Ralph Fingerhut,Johannes Häberle,Joao Matos,Mark D. Robinson,Beat Thöny,Gerald Schwank |
| Citations | 445 |
| DOI | 10.1038/s41591-018-0209-1 |
| Fields | Biochemistry, Genetics and Molecular Biology |
| Open Access | true |
| OA Status | green |
| OpenAlex ID | https://openalex.org/W2894894185 |
| PMID | 30297904 |
| Type | article |
| Year | 2018 |

## Paper authors

- [Helen Lindsay](https://scholariq.org/researchers/helen-lindsay/)

## Paper journal

- [Nature Medicine](https://scholariq.org/journals/nature-medicine/)

## Paper primary topic

- [CRISPR and Genetic Engineering](https://scholariq.org/topics/crispr-and-genetic-engineering/)

## Paper topics

- [CRISPR and Genetic Engineering](https://scholariq.org/topics/crispr-and-genetic-engineering/)
- [RNA regulation and disease](https://scholariq.org/topics/rna-regulation-and-disease/)
- [RNA and protein synthesis mechanisms](https://scholariq.org/topics/rna-and-protein-synthesis-mechanisms/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.
