# Axel Schambach

**Type:** Researchers  
**Canonical URL:** https://scholariq.org/researchers/axel-schambach/

## Facts

| Field | Value |
| --- | --- |
| Citations | 22,480 |
| Field | Virus-based gene therapy research |
| h-index | 80 |
| i10-index | 292 |
| Last Known Institution | Boston Children's Hospital |
| OpenAlex ID | https://openalex.org/A5054362291 |
| ORCID iD | 0000-0003-2743-0070 |
| Works | 589 |

## Researcher papers

Showing 12 of 13.

- [LEF-1 is crucial for neutrophil granulocytopoiesis and its expression is severely reduced in congenital neutropenia](https://scholariq.org/papers/lef-1-is-crucial-for-neutrophil-granulocytopoiesis-and-its-expression-is/)
- [Skin tissue generation by laser cell printing](https://scholariq.org/papers/skin-tissue-generation-by-laser-cell-printing/)
- [Gene Therapy for Wiskott-Aldrich Syndrome—Long-Term Efficacy and Genotoxicity](https://scholariq.org/papers/gene-therapy-for-wiskott-aldrich-syndrome-long-term-efficacy-and-genotoxicity/)
- [A Modified γ-Retrovirus Vector for X-Linked Severe Combined Immunodeficiency](https://scholariq.org/papers/a-modified-retrovirus-vector-for-x-linked-severe-combined-immunodeficiency/)
- [Insertional Transformation of Hematopoietic Cells by Self-inactivating Lentiviral and Gammaretroviral Vectors](https://scholariq.org/papers/insertional-transformation-of-hematopoietic-cells-by-self-inactivating/)
- [Long noncoding RNA <i>Chast</i> promotes cardiac remodeling](https://scholariq.org/papers/long-noncoding-rna-i-chast-i-promotes-cardiac-remodeling/)
- [A Differentiation Checkpoint Limits Hematopoietic Stem Cell Self-Renewal in Response to DNA Damage](https://scholariq.org/papers/a-differentiation-checkpoint-limits-hematopoietic-stem-cell-self-renewal-in/)
- [The phenotype of human STK4 deficiency](https://scholariq.org/papers/the-phenotype-of-human-stk4-deficiency/)
- [Cell-culture assays reveal the importance of retroviral vector design for insertional genotoxicity](https://scholariq.org/papers/cell-culture-assays-reveal-the-importance-of-retroviral-vector-design-for/)
- [Refined sgRNA efficacy prediction improves large- and small-scale CRISPR–Cas9 applications](https://scholariq.org/papers/refined-sgrna-efficacy-prediction-improves-large-and-small-scale-crispr-cas9/)
- [Equal potency of gammaretroviral and lentiviral SIN vectors for expression of O6-methylguanine–DNA methyltransferase in hematopoietic cells](https://scholariq.org/papers/equal-potency-of-gammaretroviral-and-lentiviral-sin-vectors-for-expression-of-o6/)
- [Therapeutic HNF4A mRNA attenuates liver fibrosis in a preclinical model](https://scholariq.org/papers/therapeutic-hnf4a-mrna-attenuates-liver-fibrosis-in-a-preclinical-model/)

## Researcher topics

- [Virus-based gene therapy research](https://scholariq.org/topics/virus-based-gene-therapy-research/)
- [CRISPR and Genetic Engineering](https://scholariq.org/topics/crispr-and-genetic-engineering/)
- [CAR-T cell therapy research](https://scholariq.org/topics/car-t-cell-therapy-research/)
- [RNA Interference and Gene Delivery](https://scholariq.org/topics/rna-interference-and-gene-delivery/)
- [Pluripotent Stem Cells Research](https://scholariq.org/topics/pluripotent-stem-cells-research/)

## Researcher university

- [Boston Children's Hospital](https://scholariq.org/institutions/boston-children-s-hospital/)

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Source: ScholarIQ — public research metadata, principally OpenAlex. See https://scholariq.org/sources/ for provenance and https://scholariq.org/methodology/ for what these figures mean.