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Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65 -mediated inherited retinal dystrophy: a randomised, controlled, open-label, phase 3 trial
PaperCitations, authors & open-access status
Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65 -mediated inherited retinal dystrophy: a randomised, controlled, open-label, phase 3 trial is a paper indexed in ScholarIQ from OpenAlex. ScholarIQ records 1,923 citations, 2017 year and closed oa status.
1,923
Citations
2017
Year
closed
OA Status